Brain injection gene therapy offers hope for rare neurological disorder
Disease control
Recruiting now
This early-stage trial is testing whether a single injection of experimental gene therapy (MVX-220) into the fluid around the brain can help people with Angelman syndrome. The study will enroll 12 children and adults to first check safety, then see if the treatment improves commu…
Phase: PHASE1, PHASE2 • Sponsor: MavriX Bio, LLC • Aim: Disease control
Last updated Mar 24, 2026 12:03 UTC