First human trial aims to cure sickle cell with One-Time gene therapy
⭐️ CURE ⭐️
Recruiting now
This early-stage trial is testing a new gene therapy called nula-cel for people with severe sickle cell disease. The treatment involves collecting a patient's own blood stem cells, modifying them in a lab to produce healthy hemoglobin, and then returning them to the patient. The …
Phase: PHASE1, PHASE2 • Sponsor: Kamau Therapeutics • Aim: ⭐️ CURE ⭐️
Last updated Mar 30, 2026 14:30 UTC