Could a Fatty-Acid drug help kids with rare energy disorder?
Disease control
Recruiting now
This early study is testing a drug called triheptanoin (Dojolvi) in children with pyruvate dehydrogenase complex (PDC) deficiency, a rare genetic condition that affects energy production. The trial will enroll 6 children aged 1 to 18 and look at safety, side effects, and changes …
Phase: PHASE1 • Sponsor: Jirair Krikor Bedoyan • Aim: Disease control
Last updated Jun 27, 2026 09:06 UTC