Jerry Vockley, Md, Phd
Clinical trials sponsored by Jerry Vockley, Md, Phd, explained in plain language.
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Could a urea cycle drug help MCADD patients fast longer?
Disease control TerminatedThis study tests whether sodium phenylbutyrate, a drug already approved for another condition, can help people with MCADD (a genetic disorder that affects fat breakdown). About 24 participants aged 10 and older will take the drug for 4 weeks. Researchers will check safety and see…
Phase: PHASE2 • Sponsor: Jerry Vockley, MD, PhD • Aim: Disease control
Last updated May 14, 2026 12:02 UTC
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Could a fatty acid drug stop dangerous blood sugar drops in MCADD?
Disease control TerminatedThis study tests a drug called triheptanoin in 8 adults with MCADD, a genetic condition that can cause dangerously low blood sugar. The drug is already approved for similar disorders. Researchers want to see if it is safe and helps prevent hypoglycemia during fasting. Participant…
Phase: PHASE2 • Sponsor: Jerry Vockley, MD, PhD • Aim: Disease control
Last updated May 11, 2026 20:48 UTC
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Gene test speed could save newborns in ICU
Knowledge-focused ENROLLING_BY_INVITATIONThis study looks at whether whole genome sequencing (a complete read of a person's DNA) can diagnose genetic diseases in newborns in intensive care more quickly than standard tests. About 400 newborns with suspected genetic conditions will take part. The goal is to see if faster …
Phase: NA • Sponsor: Jerry Vockley, MD, PhD • Aim: Knowledge-focused
Last updated May 07, 2026 18:42 UTC