Jerry Vockley, Md, Phd
Clinical trials sponsored by Jerry Vockley, Md, Phd, explained in plain language.
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Hope for rare disorder: drug trial aims to stop dangerous blood sugar crashes
Disease control TerminatedThis study is testing if a medication called triheptanoin can safely prevent low blood sugar (hypoglycemia) in adults with a rare inherited condition called MCADD. Eight participants will take the drug for about 9 weeks while researchers monitor for side effects and check if it h…
Phase: PHASE2 • Sponsor: Jerry Vockley, MD, PhD • Aim: Disease control
Last updated Mar 25, 2026 14:08 UTC
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Experimental drug aims to help rare metabolic disorder patients handle fasting
Disease control TerminatedThis study is testing if a medication called sodium phenylbutyrate can help people with a rare genetic disorder called MCAD deficiency. The main goal is to see if the drug allows patients to safely fast for longer periods without developing low blood sugar. The trial involves 24 …
Phase: PHASE2 • Sponsor: Jerry Vockley, MD, PhD • Aim: Disease control
Last updated Mar 12, 2026 13:51 UTC
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Racing the clock: can a Baby's full genetic code speed up diagnosis in the ICU?
Diagnosis ENROLLING_BY_INVITATIONThis study aims to see if reading a newborn's entire genetic code (whole genome sequencing) can help doctors find a diagnosis faster than standard tests when a baby is critically ill in the intensive care unit. Researchers will enroll 400 newborns and their parents to compare the…
Phase: NA • Sponsor: Jerry Vockley, MD, PhD • Aim: Diagnosis
Last updated Mar 31, 2026 12:12 UTC