Jcr Pharmaceuticals Co., Ltd.

This study continues testing JR-141 to see if it remains safe and effective for Hunter syndrome patients over the long term. It follows 80 patients who were already in the main study, tracking how their thinking skills, walking ability, and organ health change. The goal is to und…

This study is testing an investigational drug called JR-141 for Hunter syndrome (MPS II), a rare genetic disorder. It aims to see if JR-141 can better control the disease, particularly its effects on brain development and thinking skills, compared to the current standard treatmen…