Harmony Biosciences Management, Inc.
Clinical trials sponsored by Harmony Biosciences Management, Inc., explained in plain language.
-
New safety check for rare genetic disorder treatment
Disease control ENROLLING_BY_INVITATIONThis study is checking the long-term safety of a medication called pitolisant for people with Prader-Willi syndrome, a rare genetic disorder. It's open to about 150 participants who have already taken pitolisant in previous related studies. Researchers will monitor participants e…
Phase: PHASE3 • Sponsor: Harmony Biosciences Management, Inc. • Aim: Disease control
Last updated Apr 02, 2026 01:41 UTC
-
New hope for fighting crippling sleepiness in rare genetic disorder
Symptom relief OngoingThis study is testing whether a medication called pitolisant can safely reduce excessive daytime sleepiness in people with Prader-Willi syndrome (PWS), a rare genetic disorder. About 65 patients aged 6 to 65 will receive either the drug or a placebo for 11 weeks, with an option f…
Phase: PHASE2 • Sponsor: Harmony Biosciences Management, Inc. • Aim: Symptom relief
Last updated Mar 25, 2026 14:08 UTC