Gene therapy trial aims to fix copper buildup in Wilson's disease
Disease control
Not yet recruiting
This early-stage trial tests a gene therapy called GC310 for Wilson's disease, a genetic condition that causes copper buildup in the body. Researchers will give a single dose to 15 adults and monitor them for a year to check safety and whether it improves copper levels. The goal …
Phase: PHASE1, PHASE2 • Sponsor: GeneCradle Inc • Aim: Disease control
Last updated Jun 26, 2026 17:24 UTC