One-Shot gene therapy trial aims to fix copper poisoning disease
Disease control
Not yet recruiting
This is an early-stage trial testing a new, one-time gene therapy called GC310 for adults with Wilson's Disease. The main goals are to find a safe dose and see if the treatment helps the body properly manage copper, which builds up to toxic levels in this condition. About 15 part…
Phase: PHASE1, PHASE2 • Sponsor: GeneCradle Inc • Aim: Disease control
Last updated Mar 23, 2026 15:16 UTC