Gene therapy for krabbe disease: researchers track Long-Term safety and progress
Knowledge-focused
Terminated
This study follows up with Krabbe disease patients who previously received FBX-101 gene therapy in earlier clinical trials. The goal is to check for long-term side effects and see how well their motor skills are maintained over time. Only 2 participants were enrolled, and no new …
Sponsor: Forge Biologics, Inc • Aim: Knowledge-focused
Last updated May 14, 2026 12:02 UTC