Tracking the future: Long-Term watch on pioneering gene therapy for devastating childhood disease
Knowledge-focused
Terminated
This study is monitoring children with Krabbe disease who previously received an experimental gene therapy called FBX-101 in earlier trials. The goal is to track their long-term safety and see how their motor skills, thinking, and overall health change over several years. It is a…
Sponsor: Forge Biologics, Inc • Aim: Knowledge-focused
Last updated Mar 18, 2026 14:55 UTC