Stem cells injected to fight rare nerve disease
Disease control
Recruiting now
This early-phase trial tests a stem cell product called EN001 in 27 adults with Charcot-Marie-Tooth disease type 1A, a genetic nerve disorder that causes muscle weakness. The study has two parts: first, an open-label phase to check safety and find the right dose; second, a placeb…
Phase: PHASE1, PHASE2 • Sponsor: ENCell • Aim: Disease control
Last updated Jun 27, 2026 12:38 UTC