Scientists test One-Shot gene fix aiming to cure sickle cell
⭐️ CURE ⭐️
Ongoing
This is an early safety study testing a one-time gene therapy that aims to cure sickle cell disease. Doctors collect a patient's own blood stem cells, use a modified virus to insert a corrective gene, and then return the cells after chemotherapy. The goal is to see if this approa…
Phase: PHASE1 • Sponsor: David Williams • Aim: ⭐️ CURE ⭐️
Last updated Mar 30, 2026 14:29 UTC