First-Ever trial aims to stop seizures before they start in rare genetic disorder
Prevention
Recruiting now
This study is testing if a drug called sirolimus, given early in life, can prevent or delay the onset of seizures in infants diagnosed with Tuberous Sclerosis Complex (TSC). It will enroll 64 infants under 7 months old who have TSC but have not yet had seizures. The goal is to se…
Phase: PHASE2 • Sponsor: Darcy Krueger • Aim: Prevention
Last updated Mar 30, 2026 14:29 UTC