One-Time gene edit aims to cure devastating blood diseases
⭐️ CURE ⭐️
Recruiting now
This early-stage trial is testing a one-time gene editing treatment for people with severe sickle cell disease or beta-thalassemia. Doctors take a patient's own blood stem cells, edit a specific gene to boost healthy fetal hemoglobin, and return the cells after chemotherapy. The …
Phase: PHASE1 • Sponsor: Daniel Bauer • Aim: ⭐️ CURE ⭐️
Last updated Mar 27, 2026 12:38 UTC