Gene editing could cure sickle cell and thalassemia in new trial
⭐️ CURE ⭐️
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This study tests a gene therapy that edits a patient's own blood stem cells to produce more fetal hemoglobin, a healthy type that can replace the defective hemoglobin causing sickle cell disease or beta-thalassemia. The treatment involves a stem cell transplant using the patient'…
Phase: PHASE1 • Sponsor: Daniel Bauer • Aim: ⭐️ CURE ⭐️
Last updated May 06, 2026 16:14 UTC