Can a massive patient database unlock new treatments for muscular dystrophy?
Knowledge-focused
Completed
This project creates a central repository of medical records, genetic test results, and patient-reported information from people with Duchenne or Becker muscular dystrophy, as well as carriers. Anyone aged 4 weeks or older with a confirmed diagnosis can join. The goal is to provi…
Sponsor: CureDuchenne • Aim: Knowledge-focused
Last updated Jul 26, 2026 00:00 UTC