New hope for kids with rare cell disease: targeted drug trial launched
Disease control
Recruiting now
This study tests a drug called trametinib in 75 children with Langerhans cell histiocytosis (LCH), a rare disease where certain immune cells grow out of control. The goal is to see if the drug is safe and can stop the disease from getting worse. Children with newly diagnosed or r…
Phase: PHASE2 • Sponsor: Cook Children's Health Care System • Aim: Disease control
Last updated May 26, 2026 12:04 UTC