Hope for rare disorder: Two-Year drug trial tests weight and hormone benefits
Disease control
ENROLLING_BY_INVITATION
This study is testing the long-term safety and effects of a drug called theophylline in people with a rare genetic disorder called pseudohypoparathyroidism. It involves about 34 children and young adults who have already completed a previous related trial. The main goals are to s…
Phase: PHASE2 • Sponsor: Ashley Shoemaker • Aim: Disease control
Last updated Mar 23, 2026 15:14 UTC