New pompe disease drug enters early human testing
Disease control
Ongoing
This early-phase study tests a new drug called ABX1100 in healthy volunteers and people with late-onset Pompe disease. The main goal is to check if the drug is safe and how the body processes it. The study is small, with 46 participants, and is not yet testing if the drug works a…
Phase: EARLY_PHASE1 • Sponsor: Aro Biotherapeutics • Aim: Disease control
Last updated May 04, 2026 02:59 UTC