New pompe disease drug moves to first human tests
Disease control
Completed
This early-phase study tested a new drug called ABX1100 in 46 people, including healthy volunteers and patients with late-onset Pompe disease. The main goal was to check safety and how the drug moves through the body. Researchers gave single or multiple doses to find the right am…
Phase: EARLY_PHASE1 • Sponsor: Aro Biotherapeutics • Aim: Disease control
Last updated Jun 27, 2026 12:30 UTC