New pompe disease drug moves to first human tests
Disease control
Completed
This early-phase study tested a new drug called ABX1100 in 46 people, including healthy volunteers and patients with late-onset Pompe disease. The main goal was to check safety and how the drug moves through the body. Researchers gave single or multiple doses to find the right am…
Early phase 1 • Sponsor: Aro Biotherapeutics • Aim: Disease control
Last updated Jun 27, 2026 12:30 UTC