Experimental drug targets toxic sugar to halt rare nerve disease
Disease control
Ongoing
This study is testing whether a drug called AT-007 can help control a rare, inherited nerve disease called SORD deficiency. The drug aims to lower high levels of a harmful sugar alcohol (sorbitol) in the body, which is thought to damage nerves and cause walking difficulties. Abou…
Phase: PHASE2, PHASE3 • Sponsor: Applied Therapeutics, Inc. • Aim: Disease control
Last updated Mar 30, 2026 14:33 UTC