This study tests an experimental drug called AT-007 in people with a rare inherited nerve disorder (SORD deficiency) that causes weakness and walking problems. The drug aims to lower harmful sorbitol levels in cells, which build up due to the genetic defect. About 56 adults aged …
Phase: PHASE2, PHASE3 • Sponsor: Applied Therapeutics, Inc. • Aim: Disease control
Last updated May 17, 2026 11:39 UTC