Cough medicine repurposed for rare brain disease in kids
Disease control
Terminated
This study tested high doses of Ambroxol, a common cough medicine, in 12 children aged 3 to 18 with Type 3 Gaucher disease, a rare genetic disorder affecting the brain and body. The goal was to see if it is safe and can improve movement problems like ataxia. The trial took place …
Phase: NA • Sponsor: Agyany Pharma LTD • Aim: Disease control
Last updated Jun 27, 2026 12:03 UTC