Gene therapy for 'Butterfly Skin' disease tracked for 15 years in major safety registry
Disease control
Recruiting now
This registry follows people with recessive dystrophic epidermolysis bullosa (RDEB) who have been treated with prademagene zamikeracel, a gene therapy made from their own skin cells and surgically applied to wounds. The study monitors long-term safety and wound healing durability…
Sponsor: Abeona Therapeutics, Inc • Aim: Disease control
Last updated Jul 16, 2026 00:00 UTC