X-SCID

Clinical trials for X-SCID explained in plain language.

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Gene editing offers new hope for 'Bubble Boy' disease

Disease control ENROLLING_BY_INVITATION

This study tests a new gene therapy for X-linked severe combined immunodeficiency (XSCID), a rare immune disorder. Researchers collect a person's own stem cells, fix the faulty gene using base editing, and return the cells to the body. The goal is to rebuild the immune system. Th…

Matched conditions: X-SCID

Phase: PHASE1, PHASE2 • Sponsor: National Institute of Allergy and Infectious Diseases (NIAID) • Aim: Disease control

Last updated Apr 30, 2026 15:48 UTC

X-SCID

Get alerted when new X-SCID trials appear

Gene editing offers new hope for 'Bubble Boy' disease