Please sign in to follow a disease.

WHIM

Clinical trials for WHIM explained in plain language.

Never miss a new study

Get alerted when new WHIM trials appear

Sign up with your email to follow new studies for WHIM, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.

Our safety recommendation!

By submitting, you agree to our Terms of use

Not yet recruiting 1

Rewriting the code: a One-Time gene fix for a rare immune disease?

⭐️ CURE ⭐️ Not yet recruiting

This trial tests a one-time gene therapy for WHIM syndrome, a rare inherited immune disorder that causes severe infections. Doctors collect a person's own blood stem cells, use base editing to correct the faulty CXCR4 gene, and return the edited cells to the body. The goal is to …

Matched conditions: WHIM

Phase: PHASE1, PHASE2 • Sponsor: National Institute of Allergy and Infectious Diseases (NIAID) • Aim: ⭐️ CURE ⭐️

Last updated Aug 23, 2026 00:00 UTC

WHIM

Get alerted when new WHIM trials appear

Rewriting the code: a One-Time gene fix for a rare immune disease?