VANISHING WHITE MATTER DISEASE
Clinical trials for VANISHING WHITE MATTER DISEASE explained in plain language.
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New drug trial offers hope for rare brain disease
Disease control Recruiting nowThis study tests an experimental drug called fosigotifator in people with Vanishing White Matter disease, a rare genetic brain disorder. About 50 adults, children, and infants will receive the drug to see if it is safe and how the body processes it. Researchers will also look for…
Matched conditions: VANISHING WHITE MATTER DISEASE
Phase: PHASE1, PHASE2 • Sponsor: Calico Life Sciences LLC • Aim: Disease control
Last updated May 14, 2026 12:05 UTC
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Massive leukodystrophy biobank aims to unlock disease secrets
Knowledge-focused Recruiting nowThis study collects medical information and biological samples from up to 12,000 people with leukodystrophies—rare brain disorders affecting white matter. Researchers will use this data to find new genetic causes, develop biomarkers, and better understand how these diseases progr…
Matched conditions: VANISHING WHITE MATTER DISEASE
Sponsor: Children's Hospital of Philadelphia • Aim: Knowledge-focused
Last updated May 13, 2026 16:02 UTC
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Major study tracks rare brain disorders to unlock disease secrets
Knowledge-focused Recruiting nowThis study follows 1,500 people with rare genetic brain diseases to learn how these conditions progress. Researchers will track thinking, movement, and daily living skills over time. The goal is to better understand the diseases and how treatments might affect them.
Matched conditions: VANISHING WHITE MATTER DISEASE
Sponsor: University of Pittsburgh • Aim: Knowledge-focused
Last updated May 13, 2026 16:00 UTC