STEROID-REFRACTORY DIAMOND-BLACKFAN ANEMIA (DBA)

Clinical trials for STEROID-REFRACTORY DIAMOND-BLACKFAN ANEMIA (DBA) explained in plain language.

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Completed 1

New pill offers hope for patients with rare, Treatment-Resistant blood disease

Disease control Completed

This study tested a new oral drug called bitopertin for adults with Diamond-Blackfan anemia (DBA) who don't respond well to steroids. DBA is a rare, inherited condition where the bone marrow fails to make enough red blood cells, often requiring frequent transfusions. The goal was…

Matched conditions: STEROID-REFRACTORY DIAMOND-BLACKFAN ANEMIA (DBA)

Phase: PHASE1, PHASE2 • Sponsor: National Heart, Lung, and Blood Institute (NHLBI) • Aim: Disease control

Last updated Mar 19, 2026 14:55 UTC

STEROID-REFRACTORY DIAMOND-BLACKFAN ANEMIA (DBA)

Get alerted when new STEROID-REFRACTORY DIAMOND-BLACKFAN ANEMIA (DBA) trials appear

New pill offers hope for patients with rare, Treatment-Resistant blood disease