SPINAL MUSCULAR ATROPHY 1

Clinical trials for SPINAL MUSCULAR ATROPHY 1 explained in plain language.

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Not yet finished but already full! 1 Completed 1

New gene therapy tested for devastating infant muscle disease

Disease control Ongoing

This early-stage study is testing a new gene therapy called SKG0201 in infants with spinal muscular atrophy type 1, a severe genetic muscle-wasting disease. Researchers are checking if the treatment is safe and looking for early signs that it might help babies survive longer and …

Matched conditions: SPINAL MUSCULAR ATROPHY 1

Phase: NA • Sponsor: Kun Sun • Aim: Disease control

Last updated Mar 23, 2026 15:16 UTC

SPINAL MUSCULAR ATROPHY 1

Get alerted when new SPINAL MUSCULAR ATROPHY 1 trials appear

New gene therapy tested for devastating infant muscle disease