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SPASTIC PARAPLEGIA

Clinical trials for SPASTIC PARAPLEGIA explained in plain language.

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Trials to join now! 1 Completed 4

Gene therapy aims to halt rare childhood paralysis disorder

Disease control Recruiting now

This trial tests a single injection of MELPIDA, a gene therapy that delivers a working copy of the AP4M1 gene directly into the spinal fluid of children with SPG50. SPG50 is a rare genetic condition that causes muscle stiffness, intellectual disability, and developmental delays. …

Matched conditions: SPASTIC PARAPLEGIA

Phase: PHASE1, PHASE2 • Sponsor: Elpida Therapeutics SPC • Aim: Disease control

Last updated Jul 10, 2026 00:00 UTC

SPASTIC PARAPLEGIA

Get alerted when new SPASTIC PARAPLEGIA trials appear

Gene therapy aims to halt rare childhood paralysis disorder