RARE GENETIC DISORDERS
Clinical trials for RARE GENETIC DISORDERS explained in plain language.
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IPad app could give voice to kids with rare genetic disorders
Symptom relief Recruiting nowThis trial tests whether an iPad loaded with a speech-generating app can help children aged 3-12 with rare genetic conditions who have very limited speech. Each of the 38 participants will use the device during therapy sessions and also receive usual care, in a crossover design. …
Matched conditions: RARE GENETIC DISORDERS
Phase: NA • Sponsor: Murdoch Childrens Research Institute • Aim: Symptom relief
Last updated Jun 27, 2026 12:37 UTC
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Study explores the hidden toll of rare genetic diseases on families
Knowledge-focused Recruiting nowThis study looks at how the daily abilities of young children (0-4 years) with rare genetic disorders impact their families' mental health and quality of life. Researchers will assess the child's functional independence and measure parents' depression and well-being through quest…
Matched conditions: RARE GENETIC DISORDERS
Sponsor: Bahçeşehir University • Aim: Knowledge-focused
Last updated Jun 27, 2026 08:11 UTC