POSTERIOR COLUMN ATAXIA WITH RETINITIS PIGMENTOSA

Clinical trials for POSTERIOR COLUMN ATAXIA WITH RETINITIS PIGMENTOSA explained in plain language.

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First-ever single-patient trial targets rare blindness and balance disorder

Disease control ENROLLING_BY_INVITATION

This early-stage study tests a new type of genetic medicine (called an antisense oligonucleotide) in just one person with PCARP, a rare disease that causes vision loss and trouble with balance. The main goal is to see if the treatment is safe and tolerable. The participant will r…

Matched conditions: POSTERIOR COLUMN ATAXIA WITH RETINITIS PIGMENTOSA

Phase: EARLY_PHASE1 • Sponsor: University of Colorado, Denver • Aim: Disease control

Last updated May 22, 2026 14:04 UTC

POSTERIOR COLUMN ATAXIA WITH RETINITIS PIGMENTOSA

Get alerted when new POSTERIOR COLUMN ATAXIA WITH RETINITIS PIGMENTOSA trials appear

First-ever single-patient trial targets rare blindness and balance disorder