POMPE DISEASE
Clinical trials for POMPE DISEASE explained in plain language.
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New study tracks early signs of pompe in screened newborns
Knowledge-focused OngoingThis study follows 20 newborns and children who were found to have late-onset Pompe disease through newborn screening. Researchers track muscle and joint symptoms, lab results, and quality of life over several years to learn how the disease develops. No treatments are given; the …
Matched conditions: POMPE DISEASE
Sponsor: Duke University • Aim: Knowledge-focused
Last updated May 15, 2026 11:57 UTC
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New test could predict falls in muscle disease patients
Knowledge-focused ENROLLING_BY_INVITATIONThis study aims to create a simple test to predict fall risk in people with neuromuscular disorders like muscular dystrophy, ALS, and myasthenia gravis. Researchers will measure how well participants perform tasks like standing up from a chair, walking, and balancing. The goal is…
Matched conditions: POMPE DISEASE
Sponsor: LMU Klinikum • Aim: Knowledge-focused
Last updated May 07, 2026 18:39 UTC