OPTIC, ATROPHY, HEREDITARY, LEBER
Clinical trials for OPTIC, ATROPHY, HEREDITARY, LEBER explained in plain language.
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Gene therapy injection tested to halt blindness from rare genetic disease
Disease control CompletedThis Phase 3 trial tested whether a single gene therapy injection (GS010) into the eye could improve vision in people with Leber Hereditary Optic Neuropathy (LHON), a rare genetic condition that causes rapid vision loss. The study involved 37 participants who had experienced visi…
Matched conditions: OPTIC, ATROPHY, HEREDITARY, LEBER
Phase: PHASE3 • Sponsor: GenSight Biologics • Aim: Disease control
Last updated Mar 30, 2026 14:29 UTC
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Gene therapy injection tested to halt rapid blindness
Disease control CompletedThis study tested whether a single gene therapy injection (called GS010) into the eye could improve or preserve vision in people with a rare, rapidly progressing form of inherited blindness (LHON). It involved 39 participants who had started losing vision within the last 6 months…
Matched conditions: OPTIC, ATROPHY, HEREDITARY, LEBER
Phase: PHASE3 • Sponsor: GenSight Biologics • Aim: Disease control
Last updated Mar 23, 2026 15:17 UTC