NIEMANN-PICK B

Clinical trials for NIEMANN-PICK B explained in plain language.

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Not yet finished but already full! 1

New stem cell approach shows promise for rare childhood diseases

Disease control Ongoing

This study tests a stem cell transplant method for people with inherited metabolic disorders and severe osteopetrosis. The goal is to see if a donor's stem cells can successfully take over the patient's bone marrow while keeping side effects low. Participants receive chemotherapy…

Matched conditions: NIEMANN-PICK B

Phase: PHASE2 • Sponsor: Masonic Cancer Center, University of Minnesota • Aim: Disease control

Last updated May 26, 2026 10:35 UTC

NIEMANN-PICK B

Get alerted when new NIEMANN-PICK B trials appear

New stem cell approach shows promise for rare childhood diseases