NEONATAL DISEASE

Clinical trials for NEONATAL DISEASE explained in plain language.

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New hope for duchenne: targeted drug trial aims to slow muscle decline

Disease control Not yet recruiting

This study tests an experimental drug called AOC 1044 (delpacibart zotadirsen) in 70 boys aged 7 to 16 with Duchenne muscular dystrophy who have a specific genetic change (exon 44 skipping). The drug is given through a vein and aims to improve muscle function, such as how fast th…

Matched conditions: NEONATAL DISEASE

Phase: PHASE3 • Sponsor: Avidity Biosciences, Inc. • Aim: Disease control

Last updated May 15, 2026 11:57 UTC

NEONATAL DISEASE

Get alerted when new NEONATAL DISEASE trials appear

New hope for duchenne: targeted drug trial aims to slow muscle decline