MUSCULAR DYSTROPHY, DUCHENNE
Clinical trials for MUSCULAR DYSTROPHY, DUCHENNE explained in plain language.
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Gene therapy trial offers hope for boys with devastating muscle disease
Disease control Recruiting nowThis study is testing an experimental gene therapy called SRP-9001 (delandistrogene moxeparvovec) in boys with Duchenne muscular dystrophy (DMD). The main goals are to see if the one-time treatment is safe and if it helps the body produce a crucial muscle protein called dystrophi…
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Phase: PHASE1 • Sponsor: Sarepta Therapeutics, Inc. • Aim: Disease control
Last updated Mar 30, 2026 14:31 UTC
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New hope for boys with devastating muscle disease
Disease control AVAILABLEThis program provides access to an investigational drug called AOC 1044 for eligible patients with Duchenne muscular dystrophy (DMD) who have a specific genetic mutation (amenable to exon 44 skipping). It is for patients aged 6 and older who are living in the US, including those …
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated Mar 10, 2026 12:53 UTC
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Breakthrough blood test could replace risky needle for prenatal diagnosis
Diagnosis Recruiting nowThis study is evaluating a new, non-invasive blood test to diagnose serious inherited genetic disorders in unborn babies. The test analyzes tiny bits of the baby's DNA found in the mother's blood, aiming to provide a safe and accurate diagnosis as early as 9 weeks into pregnancy.…
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Sponsor: Assistance Publique - Hôpitaux de Paris • Aim: Diagnosis
Last updated Mar 30, 2026 14:30 UTC
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Fabric 'Muscle' sleeve aims to lift arms for those with muscle disease
Symptom relief Recruiting nowThis study is testing a special fabric shoulder brace designed to mimic muscle support. It aims to see if wearing this device helps people with conditions like muscular dystrophy or ALS perform arm movements needed for daily tasks, such as reaching or brushing hair. Researchers w…
Matched conditions: MUSCULAR DYSTROPHY, DUCHENNE
Phase: NA • Sponsor: Seoul National University Hospital • Aim: Symptom relief
Last updated Mar 31, 2026 12:11 UTC