MUCOPOLYSACCHARIDOSIS TYPE IIIB

Clinical trials for MUCOPOLYSACCHARIDOSIS TYPE IIIB explained in plain language.

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Trials to join now! 1

Can a weekly brain infusion slow sanfilippo syndrome?

Disease control AVAILABLE

This early-access program tests whether a weekly infusion of tralesinidase alfa directly into the brain's fluid spaces is safe and tolerable for children with Sanfilippo syndrome type B, a rare genetic disorder that causes severe neurological decline. The study enrolls about 10 c…

Matched conditions: MUCOPOLYSACCHARIDOSIS TYPE IIIB

Sponsor: Spruce Biosciences • Aim: Disease control

Last updated Jul 31, 2026 00:00 UTC

MUCOPOLYSACCHARIDOSIS TYPE IIIB

Get alerted when new MUCOPOLYSACCHARIDOSIS TYPE IIIB trials appear

Can a weekly brain infusion slow sanfilippo syndrome?