MPS IVA

Clinical trials for MPS IVA explained in plain language.

Never miss a new study

Get alerted when new MPS IVA trials appear

Sign up with your email to follow new studies for MPS IVA, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.

Our safety recommendation!

By submitting, you agree to our Terms of use

Trials to join now! 2 Not yet finished but already full! 1

Experimental growth shot tested for kids with rare bone disease

Disease control Ongoing

This early-stage study is testing whether daily injections of a medication called vosoritide can safely help children with rare genetic disorders (MPS IVA and MPS VI) grow taller. Six children aged 5-10 will receive the injections for nearly two years while researchers monitor sa…

Matched conditions: MPS IVA

Phase: PHASE1, PHASE2 • Sponsor: University of California, San Francisco • Aim: Disease control

Last updated Apr 01, 2026 14:41 UTC

MPS IVA

Get alerted when new MPS IVA trials appear

Experimental growth shot tested for kids with rare bone disease