LYSOSOMAL STORAGE DISEASE

Clinical trials for LYSOSOMAL STORAGE DISEASE explained in plain language.

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Completed 2 Terminated 1

Scientists dive into rare cholesterol disorders to uncover clues

Knowledge-focused Terminated

This study looks at rare genetic disorders where the body can't make cholesterol properly, which can cause birth defects and learning problems. Researchers collect blood, urine, and tissue samples from affected people and their families to learn more about these conditions. The g…

Matched conditions: LYSOSOMAL STORAGE DISEASE

Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) • Aim: Knowledge-focused

Last updated Aug 14, 2026 00:00 UTC

LYSOSOMAL STORAGE DISEASE

Get alerted when new LYSOSOMAL STORAGE DISEASE trials appear

Scientists dive into rare cholesterol disorders to uncover clues