LGMDR9

Clinical trials for LGMDR9 explained in plain language.

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Not yet finished but already full! 1

Experimental gene therapy targets rare muscle disease

Disease control Ongoing

This early-stage trial tests a gene therapy called ATA-100 for people with LGMDR9, a rare genetic muscle disease that causes progressive weakness. Six adults receive a single intravenous infusion of the therapy, which delivers a working copy of the FKRP gene. The main goal is to …

Matched conditions: LGMDR9

Phase: PHASE1 • Sponsor: Atamyo Therapeutics • Aim: Disease control

Last updated Jun 27, 2026 07:54 UTC

LGMDR9

Get alerted when new LGMDR9 trials appear

Experimental gene therapy targets rare muscle disease