LGMDR9

Clinical trials for LGMDR9 explained in plain language.

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Not yet finished but already full! 1

Experimental gene therapy hopes to stop rare muscle disease

Disease control Ongoing

This early-stage trial tests a new gene therapy (GNT0006) for people with a rare genetic muscle disease called LGMDR9. The study involves 6 participants who receive a single intravenous dose to deliver a working copy of the FKRP gene. The main goal is to check the treatment's saf…

Matched conditions: LGMDR9

Phase: PHASE1 • Sponsor: Atamyo Therapeutics • Aim: Disease control

Last updated May 26, 2026 12:06 UTC

LGMDR9

Get alerted when new LGMDR9 trials appear

Experimental gene therapy hopes to stop rare muscle disease