LEBER CONGENITAL AMAUROSIS
Clinical trials for LEBER CONGENITAL AMAUROSIS explained in plain language.
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Experimental eye drug hopes to restore sight in rare blindness
Disease control Recruiting nowThis phase 3 trial tests an experimental drug called sepofarsen in 32 people with Leber congenital amaurosis (LCA), a rare genetic condition that causes severe vision loss from birth. The drug is injected into one eye, while the other eye gets a placebo, to see if it safely impro…
Matched conditions: LEBER CONGENITAL AMAUROSIS
Phase: PHASE3 • Sponsor: Laboratoires Thea • Aim: Disease control
Last updated Jun 27, 2026 14:02 UTC
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Thousands join fight against blindness by sharing their stories
Knowledge-focused Recruiting nowThis registry collects information from people with inherited retinal diseases, like retinitis pigmentosa and Stargardt disease. Participants share their symptoms, family history, and genetic test results online. The goal is to help researchers understand these rare diseases and …
Matched conditions: LEBER CONGENITAL AMAUROSIS
Sponsor: Foundation Fighting Blindness • Aim: Knowledge-focused
Last updated Jun 27, 2026 12:36 UTC