LCA

Clinical trials for LCA explained in plain language.

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Can a single injection restore sight in a rare childhood blindness?

⭐️ CURE ⭐️ Ongoing

This trial tests a gene therapy called ATSN-101, given as a one-time injection under the retina, for people with Leber congenital amaurosis caused by GUCY2D gene mutations. The goal is to see if the treatment is safe and can improve vision. Participants receive the therapy in one…

Matched conditions: LCA

Phase: PHASE1, PHASE2 • Sponsor: Atsena Therapeutics Inc. • Aim: ⭐️ CURE ⭐️

Last updated Aug 05, 2026 00:00 UTC

LCA

Get alerted when new LCA trials appear

Can a single injection restore sight in a rare childhood blindness?