KRABBE DISEASE

Clinical trials for KRABBE DISEASE explained in plain language.

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Trials to join now! 3 Not yet recruiting 1 Not yet finished but already full! 4 Completed 1 Terminated 1

Gene therapy for krabbe disease: did it last?

Knowledge-focused Terminated

This study follows up on children with Krabbe disease who received a one-time gene therapy infusion (FBX-101) in earlier trials. Researchers will monitor safety and measure motor skills over time. Only 2 participants are enrolled, so results are very limited.

Matched conditions: KRABBE DISEASE

Sponsor: Forge Biologics, Inc • Aim: Knowledge-focused

Last updated Jun 26, 2026 13:47 UTC

KRABBE DISEASE

Get alerted when new KRABBE DISEASE trials appear

Gene therapy for krabbe disease: did it last?