INBORN ERRORS OF METABOLISM
Clinical trials for INBORN ERRORS OF METABOLISM explained in plain language.
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New hope for kids: drug may prevent transplant complications
Disease control Not yet recruitingThis study tests whether adding the drug vorinostat to standard care can prevent graft-versus-host disease (GVHD) in children and young adults (ages 1-26) with non-cancerous blood disorders who are getting a bone marrow transplant. GVHD is a serious complication where donor cells…
Matched conditions: INBORN ERRORS OF METABOLISM
Phase: PHASE2 • Sponsor: Sung Won Choi • Aim: Disease control
Last updated Jul 02, 2026 00:00 UTC
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Could a breath test replace blood draws for metabolic disease monitoring?
Knowledge-focused Not yet recruitingThis study measures specific substances (metabolites) in the breath and blood of people with inherited metabolic disorders, those on a special ketogenic diet for epilepsy, and healthy volunteers. The goal is to see if a simple breath test can reliably track these metabolites, pot…
Matched conditions: INBORN ERRORS OF METABOLISM
Sponsor: University Children's Hospital, Zurich • Aim: Knowledge-focused
Last updated Aug 14, 2026 00:00 UTC