HEMOPHILIA A WITH ANTI FACTOR VIII

Clinical trials for HEMOPHILIA A WITH ANTI FACTOR VIII explained in plain language.

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Completed 1

One-shot gene therapy aims to free hemophilia patients from constant infusions

Disease control Completed

This trial tests a gene therapy called valoctocogene roxaparvovec for people with severe hemophilia A who have developed inhibitors (antibodies that block standard treatment). The therapy uses a harmless virus to deliver a working copy of the gene for clotting factor VIII, so the…

Matched conditions: HEMOPHILIA A WITH ANTI FACTOR VIII

Phase: PHASE1, PHASE2 • Sponsor: BioMarin Pharmaceutical • Aim: Disease control

Last updated Jul 12, 2026 00:00 UTC

HEMOPHILIA A WITH ANTI FACTOR VIII

Get alerted when new HEMOPHILIA A WITH ANTI FACTOR VIII trials appear

One-shot gene therapy aims to free hemophilia patients from constant infusions