GAUCHER'S DISEASE TYPE III

Clinical trials for GAUCHER'S DISEASE TYPE III explained in plain language.

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Not yet finished but already full! 1 Completed 1

New hope for kids with rare genetic disorder

Disease control Completed

This study tested a daily pill called eliglustat in children aged 2 to 18 with Gaucher disease, a rare genetic condition. It aimed to see if the drug was safe, how the body processed it, and if it could help control the disease by improving blood counts, organ size, and bone heal…

Matched conditions: GAUCHER'S DISEASE TYPE III

Phase: PHASE3 • Sponsor: Sanofi • Aim: Disease control

Last updated Mar 30, 2026 14:32 UTC

GAUCHER'S DISEASE TYPE III

Get alerted when new GAUCHER'S DISEASE TYPE III trials appear

New hope for kids with rare genetic disorder