DUCHENNE MUSCULAR DYSTROPHY

Clinical trials for DUCHENNE MUSCULAR DYSTROPHY explained in plain language.

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Trials to join now! 20 Not yet recruiting 1 Not yet finished but already full! 19 Completed 9 Terminated 6

New study aims to prevent liver damage in duchenne gene therapy

Disease control Not yet recruiting

This study tests whether adding sirolimus to ELEVIDYS treatment can prevent serious liver injury in boys with Duchenne muscular dystrophy. About 20 participants will receive the drug combination and be monitored for side effects. The goal is to make an existing gene therapy safer…

Matched conditions: DUCHENNE MUSCULAR DYSTROPHY

Phase: PHASE4 • Sponsor: Sarepta Therapeutics, Inc. • Aim: Disease control

Last updated May 14, 2026 12:06 UTC

DUCHENNE MUSCULAR DYSTROPHY

Get alerted when new DUCHENNE MUSCULAR DYSTROPHY trials appear

New study aims to prevent liver damage in duchenne gene therapy