CONGENITAL MYOTONIC DYSTROPHY

Clinical trials for CONGENITAL MYOTONIC DYSTROPHY explained in plain language.

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Trials to join now! 1 Completed 1

Hope for kids with rare muscle disease in drug trial

Disease control Completed

This study tested whether a drug called tideglusib could help children and teenagers (ages 6-16) with congenital myotonic dystrophy, a rare genetic muscle disease. Researchers compared tideglusib to a placebo (inactive pill) to see if it could improve symptoms, daily function, an…

Matched conditions: CONGENITAL MYOTONIC DYSTROPHY

Phase: PHASE2, PHASE3 • Sponsor: AMO Pharma Limited • Aim: Disease control

Last updated Mar 27, 2026 12:39 UTC

CONGENITAL MYOTONIC DYSTROPHY

Get alerted when new CONGENITAL MYOTONIC DYSTROPHY trials appear

Hope for kids with rare muscle disease in drug trial