CLASSIC GALACTOSEMIA
Clinical trials for CLASSIC GALACTOSEMIA explained in plain language.
Never miss a new study
Get alerted when new CLASSIC GALACTOSEMIA trials appear
Sign up with your email to follow new studies for CLASSIC GALACTOSEMIA, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
New hope for kids with rare sugar disorder: drug shows promise in trial
Disease control CompletedThis study tested an experimental drug called AT-007 in 47 children aged 2 to 18 with Classic Galactosemia, a rare genetic disorder that makes it hard to break down a sugar called galactose. The goal was to see if the drug could improve behavior, daily living skills, and language…
Matched conditions: CLASSIC GALACTOSEMIA
Phase: PHASE2, PHASE3 • Sponsor: Applied Therapeutics, Inc. • Aim: Disease control
Last updated Jun 27, 2026 07:55 UTC
-
Babble boot camp: could early talk therapy stop speech delays in rare disease?
Prevention CompletedThis study tested a program called Babble Boot Camp for babies with classic galactosemia, a rare condition that often causes speech and language problems. The program started when babies were 2 to 24 months old and involved weekly online coaching for parents from a speech therapi…
Matched conditions: CLASSIC GALACTOSEMIA
Phase: EARLY_PHASE1 • Sponsor: Arizona State University • Aim: Prevention
Last updated Jun 27, 2026 08:13 UTC