BONE MARROW FAILURE SYNDROME

Clinical trials for BONE MARROW FAILURE SYNDROME explained in plain language.

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Trials to join now! 1 Not yet recruiting 1 Not yet finished but already full! 1 Completed 1

First step toward gene therapy: stem cell collection tested in rare blood disorders

Knowledge-focused Not yet recruiting

This early-phase study tests whether it is safe and possible to collect blood stem cells from 12 people aged 18-25 with bone marrow failure syndromes. Participants receive two drugs (Filgrastim and plerixafor) to move stem cells into the bloodstream for collection. The goal is to…

Matched conditions: BONE MARROW FAILURE SYNDROME

Phase: PHASE1 • Sponsor: St. Jude Children's Research Hospital • Aim: Knowledge-focused

Last updated May 17, 2026 05:29 UTC

BONE MARROW FAILURE SYNDROME

Get alerted when new BONE MARROW FAILURE SYNDROME trials appear

First step toward gene therapy: stem cell collection tested in rare blood disorders