BATTEN'S DISEASE

Clinical trials for BATTEN'S DISEASE explained in plain language.

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Trials to join now! 1 Not yet recruiting 1

Experimental gene therapy aims to halt rare childhood brain disease

Disease control Not yet recruiting

This early-phase trial tests a gene therapy for children with CLN6 Batten disease, a rare and fatal brain disorder. Twelve children will receive a single injection of the therapy into the fluid around the spinal cord. Researchers will check if it is safe and if it can slow the di…

Matched conditions: BATTEN'S DISEASE

Phase: PHASE1, PHASE2 • Sponsor: The Charlotte and Gwenyth Gray Foundation • Aim: Disease control

Last updated Jun 27, 2026 12:34 UTC

BATTEN'S DISEASE

Get alerted when new BATTEN'S DISEASE trials appear

Experimental gene therapy aims to halt rare childhood brain disease